BILL ANALYSIS                                                                                                                                                                                                    Ó



                                                                      



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          |SENATE RULES COMMITTEE            |                   AB 395|
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                                 THIRD READING


          Bill No:  AB 395
          Author:   Pan (D)
          Amended:  05/27/11 in Assembly
          Vote:     21

           
           SENATE HEALTH COMMITTEE  :  9-0, 7/6/11
          AYES:  Hernandez, Strickland, Alquist, Anderson, Blakeslee, 
            De León, DeSaulnier, Rubio, Wolk

           SENATE APPROPRIATIONS COMMITTEE  :  9-0, 8/25/11
          AYES:  Kehoe, Walters, Alquist, Emmerson, Lieu, Pavley, 
            Price, Runner, Steinberg

           ASSEMBLY FLOOR  : 71-4, 06/01/11 - See last page for vote


           SUBJECT  :    Newborn screening program

           SOURCE  :     March of Dimes


           DIGEST  :    This bill requires the Department of Public 
          Health to expand statewide screening of newborns to include 
          screening for severe combined immunodeficiency (SCID) and 
          other T-cell lymphopenias detectable as a result of SCID.

           ANALYSIS  :    

          Existing law:

          1. Declares the intent of the Legislature that the state's 
             hereditary disorders program activities are to be fully 
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             supported by fees collected for services provided by the 
             program, unless otherwise provided. 

          2. Requires Department of Public Health (DPH) to establish 
             a genetic disease unit to coordinate programs in the 
             area of genetic disease and evaluate and prepare 
             recommendations on the implementation of tests for the 
             detection of certain hereditary and congenital diseases. 


          3. Requires DPH to charge a fee for newborn screening and 
             follow-up services, and requires the amount of the fee 
             to be established pursuant to regulation and 
             periodically adjusted. 

          4. Requires that any fee charged for screening and 
             follow-up services provided to Medi-Cal eligible 
             persons, health care service plan enrollees, or persons 
             covered by disability insurance policies are to be paid 
             directly to the Genetic Disease Testing Fund, and are 
             subject to the terms and conditions of the health care 
             service plan or insurance coverage. 

          This bill requires DPH to expand statewide screening of 
          newborns to include screening for severe SCID and other 
          T-cell lymphopenias detectable as a result of SCID.

           Background
           
           SCID  .  The defining characteristic of SCID is the absence 
          of T-cells and, as a result, the lack of B-cell functions.  
          B-cells are specialized white blood cells made in the bone 
          marrow that fight infection.  These genetic defects lead to 
          extreme susceptibility to serious illness.  Unless these 
          defects are corrected, children are vulnerable to 
          opportunistic infections and will likely die before their 
          first or second birthday.  In the past, children with this 
          disorder were kept in strict isolation, sometime in a 
          plastic isolator or "bubble."  Now treatments are available 
          to significantly enhance the health outcomes of infants 
          with SCID who are presyptomatic or early symptomatic.  

          Based on national studies, stem cells from either umbilical 
          cord blood or bone marrow appears to be effective in 

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          significantly decreasing the morbidity and mortality for 
          children with a type of SCID caused by a mutated gene on 
          the X chromosome.  According to the genetic disease 
          screening program, if the treatment is provided within 3.5 
          months of life, the long-term survival rate is 95 percent 
          and after 3.5 months it is 60 to 70 percent.  When left 
          untreated, children rarely survive past the age of two.

           Pilot project  .  Beginning in August of 2010, DPH has been 
          participating in a pilot project to test for SCID sponsored 
          by the Jeffrey Modell Foundation and the National 
          Institutes of Health.  According to the March of Dimes, all 
          babies born in California since the pilot began have been 
          screened.  Out of 235,686 babies screened, seven have been 
          identified as SCID babies.  The pilot has also lead to the 
          identification of four other babies with T-cell 
          lymphopenia.  Current data as a result of the pilot has 
          shown the rate of SCID to be 1 in 35,000 in California 
          while it was previously estimated to be 1 in 100,000.
           
          Methodology for adding new conditions  .  According to DPH, 
          there is no national standard process to add a disorder to 
          a state's screening program.  Some states will add a 
          disorder once it is recommended by the Secretary's Advisory 
          Committee on Heritable Disorders in Newborns and Children 
          (SACHDNC) but prior to official acceptance by the Health 
          and Human Services (HHS) Secretary, while other states wait 
          for the official acceptance by the HHS Secretary.  In 
          California disorders have been added through the budget 
          process or through legislation directing the department to 
          add a specific disorder to the screening program.  

          In May 2010, Secretary Sebelius of the HHS adopted the 
          SACHDNC recommendation of the Uniform Screening Panel to 
          adopt the recommendation to add SCID as a core condition 
          and the related T-cell lymphocyte deficiencies to the list 
          of secondary targets.  

           FISCAL EFFECT  :    Appropriation:  No   Fiscal Com.:  Yes   
          Local:  No

          According to the Senate Appropriations Committee:

                           Fiscal Impact (in thousands)

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             Major Provisions        2011-12   2012-13     2013-14    Fund  

            Increased DPH         $2,600   $5,300    $5,300   
            Special*
            testing costs

            Fee revenue           ($2,600) ($5,300)  ($5,300) 
            Special*

            Approximate Medi-              $650      $1,300   
            $1,300General/**
            Cal fee payments      $650     $1,300    $1,300   Federal

            Potential publicly             likely in the tens of 
            thousands to          General/
            funded health program          hundreds of thousands of 
            dollars               Federal/
            cost avoidance        per child over time         County

             *    Birth Defects Monitoring Program Fund
             **   Costs shared 50 percent federal funds, 50 percent 
               General Fund
           
           SUPPORT  :   (Verified  8/25/11)

          March of Dimes (source)
          American Academy of Pediatrics, California
          American College of Obstetricians and Gynecologists, 
          California
          California Medical Association
          Children's Advocacy Institute
          Talecris Biotherapeutics

           ARGUMENTS IN SUPPORT  :    The March of Dimes, the sponsor of 
          this bill, writes that, any disease affecting newborns that 
          can be detected and treated should be, and it is critical 
          that SCID be added to the California NBS Program.  The 
          March of Dimes argues that the health benefits of screening 
          newborns for SCID are apparent, but screening would also 
          likely lead to economic relief in California as well.  The 
          Children's Advocacy Institute writes that this bill  makes 
          possible the identification of SCID shortly after birth, 
          allowing for timely, cost-effective treatment and could 

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          save the lives of children who are born with this 
          condition.  

          The American Academy of Pediatrics writes that early 
          screening for SCID is critically important as data shows 
          that SCID infants who receive a related donor bone marrow 
          transplant within the first 14 weeks of life are 
          significantly more likely to survive and have fewer 
          problems over time than those who receive transplants later 
          in infancy or who have already developed an infection.


           ASSEMBLY FLOOR  : 
          AYES:  Achadjian, Alejo, Allen, Ammiano, Atkins, Beall, 
            Block, Blumenfield, Bonilla, Bradford, Brownley, 
            Buchanan, Butler, Charles Calderon, Campos, Carter, 
            Cedillo, Chesbro, Conway, Cook, Davis, Dickinson, Eng, 
            Feuer, Fletcher, Fong, Fuentes, Furutani, Beth Gaines, 
            Galgiani, Gatto, Gordon, Grove, Hagman, Halderman, Hall, 
            Harkey, Hayashi, Roger Hernández, Hill, Huber, Hueso, 
            Huffman, Lara, Logue, Bonnie Lowenthal, Ma, Mendoza, 
            Miller, Mitchell, Monning, Morrell, Nestande, Nielsen, 
            Norby, Olsen, Pan, Perea, Portantino, Silva, Skinner, 
            Smyth, Solorio, Swanson, Torres, Valadao, Wagner, 
            Wieckowski, Williams, Yamada, John A. Pérez
          NOES:  Bill Berryhill, Donnelly, Jones, Knight
          NO VOTE RECORDED:  Garrick, Gorell, Jeffries, Mansoor, V. 
            Manuel Pérez


          CTW:do  8/26/11   Senate Floor Analyses 

                         SUPPORT/OPPOSITION:  SEE ABOVE

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