BILL ANALYSIS                                                                                                                                                                                                    �



                                                                  AB 58
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          Date of Hearing:  March 19, 2013

                            ASSEMBLY COMMITTEE ON HEALTH
                                 Richard Pan, Chair
                 AB 58 (Wieckowski) - As Amended:  February 27, 2013
           
          SUBJECT  :  Medical experiments: human subjects.

           SUMMARY  :  Makes permanent an exemption in current law that  
          allows, until January 1, 2014, patients in life-threatening  
          emergencies to receive medical experimental treatment without  
          informed consent if specified conditions are met.

           EXISTING STATE LAW  :

          1)Establishes the Protection of Human Subjects in Medical  
            Experimentation Act (Act) which prescribes various protections  
            for subjects of medical experimentation relating to a bill of  
            rights; informed consent procedures and documentation; and,  
            the provision of specified disclosures, including the right  
            for a subject to give or withdraw consent freely and without  
            duress.  Imposes penalties for violations of these  
            protections.

          2)Exempts from the Act, until January 1, 2014, any medical  
            experimental treatment that benefits a patient subject to a  
            life-threatening emergency if all of the following conditions  
            are met:

             a)   Care is provided in accordance with the procedures and  
               additional protections of the rights and welfare of the  
               patient established by federal regulations;
             b)   The patient is in a life-threatening situation,  
               necessitating urgent intervention and available treatments  
               are unproven or unsatisfactory;
             c)   The patient is unable to give informed consent as a  
               result of the patient's medical condition;
             d)   Obtaining informed consent from the patient's legally  
               authorized representative is not feasible before the  
               treatment must be administered;
             e)   There is no reasonable way to identify prospectively the  
               individuals likely to become eligible for participation in  
               the clinical investigation; and, 
             f)   Valid scientific studies have been conducted that  
               support the potential for the intervention to provide a  








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               direct benefit to the patient.
           
          EXISTING FEDERAL LAW  :

          1)Establishes various procedures and protections relating to the  
            use of human subjects in medical research, including a  
            requirement that an investigator obtain the legally effective  
            informed consent of the subject or the subject's legally  
            authorized representative prior to involving a human being as  
            a subject in research. 

          2)Provides an exception from general requirements governing  
            informed consent of human subjects when both the investigator  
            and a physician who is not otherwise participating in the  
            clinical investigation certify all of the following in  
            writing:

             a)   The human subject is confronted by a life-threatening  
               situation necessitating the use of experimental treatment;
             b)   Informed consent cannot be obtained from the subject  
               because of an inability to communicate with, or obtain  
               legally effective consent from, the subject; 
             c)   Time is not sufficient to obtain consent from the  
               subject's legal representative; and,
             d)   There is no available alternative method of approved or  
               generally recognized therapy that provides an equal or  
               greater likelihood of saving the life of the subject.

          3)Establishes a narrow exception to existing informed consent  
            requirements to permit a limited class of research in  
            emergency settings without consent under the following  
            criteria:

             a)   The human subjects are in a life-threatening situation;
             b)   Obtaining consent is not feasible;
             c)   Participation in the research holds out the prospect of  
               direct benefit to the subjects;
             d)   The clinical investigation could not practicably be  
               carried out without the waiver of consent;
             e)   The proposed investigational plan defines the length of  
               the potential therapeutic window based on scientific  
               evidence, and the investigator has committed to attempting  
               to contact a legally authorized representative for each  
               subject within that window of time and, if feasible, to  
               asking the legally authorized representative contacted for  








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               consent within that window, rather than proceeding without  
               consent;
             f)   Informed consent procedures and documents have been  
               reviewed and approved by an institutional review board  
               (IRB) and used with subjects or their legally authorized  
               representatives in situations where use of such procedures  
               and documents is feasible; and,
             g)   Additional protections of the rights and welfare of  
               subjects will be provided, including specified  
               consultations, public disclosures, and the establishment of  
               an independent data monitoring committee.

          4)Imposes civil and criminal penalties for performing  
            unauthorized medical treatment.

           FISCAL EFFECT  :   None

           COMMENTS  :

           1)PURPOSE OF THIS BILL  .  According to the author, few emergency  
            medical interventions for the treatment of acute,  
            time-sensitive conditions, such as heart attacks, stroke,  
            shock states, seizures, and traumatic brain injury, have been  
            rigorously studied in clinical trials because patients with  
            these conditions are often unresponsive and unable to consent  
            to participate in research.  The author argues that this bill  
            aligns state law with federal requirements for emergency care  
            research studies where informed consent cannot be obtained  
            from patients experiencing these life-threatening conditions.   
            The author notes that federal law governing this exemption  
            from informed consent does not contain a sunset and this same  
            narrow exception has been granted in California for the last  
            15 years, providing ample time to extensively demonstrate the  
            benefits of this research without any evidence of harm.  The  
            author states that this bill is needed to remove the sunset  
            and allow critical, potentially life-saving emergency care  
            research studies to continue to be performed in rare instances  
            where an exception to informed consent is necessary.    

           2)EMERGENCY CARE RESEARCH  .  A 2012 booklet published by the  
            American College of Emergency Physicians, entitled "Emergency  
            Care Research: A Primer," states that emergency care research  
            is characterized by its focus on the timing, severity and  
            acute sensitivity of certain critical conditions, such as  
            stroke, trauma, shock, cardiac arrest, and respiratory  








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            failure, and the treatments capable of halting or reversing  
            them.  Because patients with these conditions are often  
            unstable and incapable of providing consent and the treatments  
            being studied take place in an ambulance or immediately on  
            arrival in the emergency department, clinical trials of  
            emergency care research can only be performed under federal  
            regulations developed by the federal Food and Drug  
            Administration (FDA) that allow for an exception from informed  
            consent for these emergency circumstances.  According to a  
            list provided by the sponsor of this bill, the California  
            Chapter of the American College of Emergency Physicians  
            (California ACEP), approximately 15 studies to date have been  
            performed since the federal exemption from informed consent  
            was established in 1996.  Research from these studies has  
            focused on improving the timely delivery of known drugs or  
            testing new treatment methods to improve the lives of  
            emergency patients.  One clinical trial utilizing the  
            exemption is currently underway in three hospitals in  
            California: UC San Francisco, Stanford, and Santa Clara Valley  
            Medical Center.  It is a study of the use of the hormone  
            progesterone in the treatment of traumatic brain injury and is  
            scheduled to continue until 2015.  

           3)EXISTING INFORMED CONSENT REQUIREMENTS  .  Federal regulations  
            for the protection of human subjects in research generally  
            prohibit an investigator from involving individuals in  
            research unless the investigator has obtained the legally  
            effective informed consent of the subject or the subject's  
            legally authorized representative.  An investigator is  
            required to seek such consent only under circumstances that  
            provide the potential subject or the representative sufficient  
            opportunity to consider whether or not to participate and  
            minimize the possibility of coercion or undue influence.   
            Information given to the subject or the representative must be  
            in language that is understandable to the subject or the  
            representative.  Informed consent, whether oral or written, is  
            prohibited from including any language in which the subject or  
            the representative is made to waive, or appear to waive, any  
            of the subject's rights, or to release, or appear to release,  
            the investigator, the sponsor, the institution, or its agents  
            from liability for negligence.

          Federal criteria allowing informed consent requirements to be  
            waived for research activities involving human subjects in  
            life-threatening situations define life-threatening as  








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            diseases or conditions where the likelihood of death is high  
            unless the course of the disease or condition is interrupted.   
            Among the criteria that must be met for the exception to apply  
            is the requirement that the sponsor of the research use  
            available data to specify the therapeutic window during which  
            the administration of the treatment to the patient should be  
            initiated.  While there is no set time for a therapeutic  
            window, it is generally identified as the time period, based  
            on available scientific evidence, during which administration  
            of the experimental treatment might reasonably produce a  
            demonstrable clinical benefit.  The therapeutic window is also  
            important because it is used as the window of time during  
            which the investigator must attempt to contact and, if  
            feasible, obtain informed consent from a patient's legally  
            authorized representative.  Additionally, in order for any  
            emergency care research to qualify for the exemption, the  
            community where the research is being conducted must be  
            consulted and notified through various forms of public  
            disclosure, such as via the newspaper, radio, television,  
            community newsletter, and/or a public website, that informed  
            consent will not be obtained for most study enrollees.

          The subject of this bill is unrelated to a recent controversy  
            surrounding two neurosurgeons from the University of  
            California, Davis (UC Davis) who performed an experimental  
            procedure on patients with brain cancer.  In these cases, the  
            neurosurgeons obtained informed consent from the patients but  
            what was not communicated to the patients was that the  
            procedure had not been approved by the FDA as an  
            investigational new treatment for testing in human subjects or  
            by UC Davis' IRB.  In response to these incidences, UC Davis  
            has since instituted an "anti-innovative use" policy that  
            expressly prohibits any use of a non-FDA approved drug,  
            biologic, or device without formal IRB and, as required, FDA  
            approval, regardless of the purpose of the use.
            
           4)IRBs  .  The exception from informed consent requirements for  
            research in emergency settings is conditional upon documented  
            findings by an IRB.  The IRB is responsible for determining  
            whether or not the criteria for allowing research in emergency  
            situations without consent have been met.  The sponsor of a  
            clinical trial for which an exception has been requested is  
            required to submit their research proposal to the IRB.  The  
            IRB must consult with representatives of the communities in  
            which the clinical investigations will be conducted and from  








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            which the subjects will be drawn to ensure that the public has  
            been appropriately notified of plans for the investigation and  
            its risks and expected benefits.  The IRB is tasked with  
            taking the community's opinions and concerns into  
            consideration when deciding whether to modify, approve, or  
            disapprove the proposed clinical trial.  The IRB must also  
            ensure that procedures are in place to provide information  
            about the clinical trial at the earliest feasible opportunity  
            to the patient, should he or she recover from the  
            life-threatening condition, or to the patient's legally  
            authorized representative.  A patient, or the patient's  
            representative, may opt to no longer participate at any point  
            in the clinical trial.

          Additionally, the IRB must find and document that an independent  
            data monitoring committee has been established to exercise  
            oversight of the clinical investigation.  The data monitoring  
            committee is established as an advisory body by the sponsor of  
            the research and is comprised of individuals not otherwise  
            connected with the particular clinical investigation.  The  
            committee is responsible for ensuring the ongoing safety of  
            current and prospective trial subjects as well as monitoring  
            the continuing validity and scientific merit of the trial.

           5)SUPPORT  .  California ACEP writes in support that, without this  
            bill, life-saving research that protects patient rights and  
            recognizes the potential for medical progress could no longer  
            take place in California.  Other supporters, such as the  
            Society for Academic Emergency Medicine, the San Francisco  
            Neurological Emergencies Treatment Trials Network, and  
            University of California, note that the very narrow  
            circumstances when urgent medical intervention can be  
            delivered without informed consent allowed under existing  
            state and federal law include sufficient safeguards for the  
            rights of medically vulnerable patients and this bill will  
            allow critical research to continue to be done to advance  
            knowledge in treating critically ill or injured patients.  The  
            Los Angeles Biomedical Research Institute points out that  
            permanently lifting the sunset on this narrow exception will  
            ensure that vital medical research continues to be conducted  
            to develop and evaluate promising new therapies for  
            Californians afflicted with sudden, unpredictable, and  
            devastating injuries and illnesses that threaten their lives  
            or lead to permanent disability.  The Civil Justice  
            Association of California adds that this bill is a common  








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            sense measure that reinforces the state's strong policy of  
            encouraging the provision of emergency assistance and  
            treatment.   
           
           6)PRIOR LEGISLATION  .

             a)   SB 1187 (Tony Strickland), Chapter 108, Statutes of  
               2010, extends to January 1, 2014, the sunset on the  
               exception in current law that waives informed consent  
               requirements for medical experimental treatment that  
               benefits a patient in a life-threatening emergency, if  
               specified conditions are met.

             b)   SB 1188 (Committee on Health and Human Services),  
               Chapter 122, Statutes of 2001, extended the sunset to  
               January 1, 2011.

             c)   SB 160 (Watson), Chapter 68, Statutes of 1997,  
               established the exemption in state law until January 1,  
               2001.

           7)AUTHOR'S AMENDMENTS  .  The author will offer the following  
            amendments in committee to mirror existing federal  
            requirements governing the exemption from informed consent for  
            emergency research relating to the role of the IRB, community  
            consultation, public disclosure, and establishment of an  
            independent data monitoring committee to oversee the research:

                 On page 2, below line 33 insert:

                 (7) The institutional review board (IRB) has  
                 reviewed and approved informed consent procedures  
                 and these procedures are to be used with subjects or  
                 their legally authorized representatives in  
                 situations where use of such procedures is feasible.  


                 (8) Additional protections of the rights and welfare  
                 of the subjects will be provided, including, at  
                 least: 

                           (a) consultation (including, where  
                 appropriate, consultation carried out by the IRB)  
                 with representatives of the communities in which the  
                 research will be conducted and from which the  








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                 subjects will be drawn;

                           (b) public disclosure to the communities  
                 in which the research will be conducted and from  
                 which the subjects will be drawn, prior to  
                 initiation of the research, of plans for the  
                 research and its risks and expected benefits;

                           (c) public disclosure of sufficient  
                 information following completion of the research to  
                 apprise the community and researchers of the study,  
                 including the demographic characteristics of the  
                 research population, and its results; and,

                           (d) establishment of an independent data  
                 monitoring committee to exercise oversight of the  
                 research.  

           REGISTERED SUPPORT / OPPOSITION  :  

           Support 
           
          California Chapter of the American College of Emergency  
          Physicians (sponsor)
          BIOCOM
          Civil Justice Association of California
          Los Angeles Biomedical Research Institute
          San Francisco Neurological Emergencies Treatment Trials Network
          Society for Academic Emergency Medicine
          University of California

           Opposition 
           
          None on file.
           
          Analysis Prepared by  :    Cassie Royce / HEALTH / (916) 319-2097