BILL ANALYSIS                                                                                                                                                                                                    �






                             SENATE COMMITTEE ON HEALTH
                          Senator Ed Hernandez, O.D., Chair

          BILL NO:       SB 598
          AUTHOR:        Hill
          AMENDED:       April 16, 2013
          HEARING DATE:  May 1, 2013
          CONSULTANT:    Moreno

           SUBJECT  :  Biosimilars.
           
          SUMMARY  :  Permits a pharmacist filling a prescription order for  
          a prescribed biological product to select a biosimilar only if  
          certain conditions are met.  

          Existing federal law:
          1.Requires drug manufacturers to obtain approval of new drugs  
            from the federal Food and Drug Administration (FDA).  

          2.Prohibits a person from delivering for introduction into  
            interstate commerce any biological product unless a license is  
            issued pursuant to the Public Health Service Act (PHSA).  

          3.Creates an abbreviated pathway for biological products that  
            are similar to or interchangeable with licensed biological  
            products, known as the Biologics Price Competition and  
            Innovation Act of 2009 (BPCIA).  

          4.Requires that, for a biological product to be considered  
            biosimilar to a reference product, data must be derived from  
            analytical, animal and clinical studies as specified.  

          5.Clarifies that a product is biosimilar to a reference product  
            under the BPCIA if the proposed biosimilar product is highly  
            similar to the reference product notwithstanding minor  
            differences in clinically inactive components and that no  
            clinically meaningful differences exist between the proposed  
            biosimilar product and the reference product in terms of  
            safety, purity and potency.  

          Existing state law: 
          1.Establishes the Food and Drug Branch (FDB) within the  
            California Department of Public Health (DPH) to assure that  
            foods, drugs, medical devices, cosmetics and certain other  
            consumer products are safe and are not adulterated, misbranded  
            nor falsely advertised; and that drugs and medical devices are  
                                                         Continued---



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            effective.

          2.Defines biologics as human whole blood; human whole blood  
            derivatives specified by regulations; serum, vaccine, live  
            vaccine, killed vaccine, tissue vaccine, autogenous vaccine,  
            live virus, killed virus, live bacterial culture, killed  
            bacterial culture, bacterin, hormone, tissue extract, gland  
            extract, gland preparation, insulin, and similar products made  
            from human or animal tissues or micro-organisms.   

          3.Under the Pharmacy Law, provides for the licensure and  
            regulation of pharmacies, pharmacists and wholesalers of  
            dangerous drugs or devices by the Board within the Department  
            of Consumer Affairs (DCA).  

          4.Specifies certain requirements regarding the dispensing and  
            furnishing of dangerous drugs and devices, and prohibits a  
            person from furnishing any dangerous drug or device except  
            upon the prescription of a physician, dentist, podiatrist,  
            optometrist, veterinarian or naturopathic doctor.  

          5.Authorizes pharmacists filling prescription orders for drug  
            products prescribed by their trade or brand names to  
            substitute generic drugs for orders if the generic contains  
            the same active chemical ingredients of equivalent strength  
            and duration of therapy, subject to a patient notification and  
            bottle labeling requirement, unless the prescriber specifies  
            that a pharmacist may not substitute another drug product by  
            either indicating on the form submitted for the filling of the  
            prescription drug orders "Do not substitute" or words of  
            similar meaning or selecting a box on the form marked "Do not  
            substitute."  

          6.Authorizes pharmacists filling prescription orders for drug  
            products prescribed by their trade or brand names to  
            substitute a drug product with a different form of medication  
            with the same active chemical ingredients of equivalent  
            strength and duration of therapy as the prescribed drug  
            product when the change will improve the ability of the  
            patient to comply with the prescribed drug therapy, subject to  
            a patient notification and bottle labeling requirement, unless  
            the prescriber specifies that a pharmacist may not substitute  
            another drug product by either indicating on the form  
            submitted for the filling of the prescription drug orders "Do  
            not substitute" or words of similar meaning or selecting a box  
            on the form marked "Do not substitute."  




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          This bill:
          1.Permits a pharmacist filling a prescription order for a  
            prescribed biological product to select a biosimilar only if:

             a.   The product selected as a biosimilar has been approved  
               by the federal Food and Drug Administration (FDA), as  
               specified, and has been determined to be interchangeable  
               with the prescribed biological product;
             b.   The prescriber does not personally indicate, either  
               orally or in his or her own handwriting, "Do not  
               substitute," or words of similar meaning;
             c.   For prescriptions filled prior to January 1, 2017, the  
               pharmacy notifies the prescriber or enters the appropriate  
               information in a patient record system shared by the  
               prescriber within five business days of the selection; and,
             d.   For prescriptions filled prior to January 1, 2017, the  
               pharmacy retains a written record of the biosimilar  
               selection for a period of at least three years.

          2.Prohibits a selection from being made pursuant to this bill if  
            the prescriber personally indicates, either orally or in his  
            or her own handwriting, "Do not substitute," or words of  
            similar meaning. Specifies that nothing in the bill prohibits  
            a prescriber from checking a box on a prescription marked "Do  
            not substitute" if the prescriber personally checkmarks or  
            initials the box.

          3.Requires selection pursuant to this bill to be within the  
            discretion of the pharmacist, except as specified.  Requires  
            the pharmacist who selects the biosimilar to be dispensed to  
            assume the same responsibility for substituting the dispensed  
            biosimilar as would be incurred in filling a prescription for  
            a biosimilar using the prescribed form of medication.   
            Prohibits there from being any liability on the prescriber for  
            an act or omission by a pharmacist in selecting, preparing, or  
            dispensing a drug product pursuant to this section.

          4.Requires this bill to apply to all prescriptions, including  
            those presented by or on behalf of persons receiving  
            assistance from the federal government or under Medi-Cal

          5.Requires the substitution of a biosimilar, when a selection is  
            made pursuant to this bill, to be communicated to the patient.





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          6.Requires the Board of Pharmacy to maintain on its public  
            Internet Web site a link to the current list, if available, of  
            biosimilar products determined by the FDA to be  
            interchangeable.

           FISCAL EFFECT  :  This bill has not been analyzed by a fiscal  
          committee.

           COMMENTS  :  
           1.Author's statement.  SB 598 allows less expensive biosimilar  
            medicines to be substituted by pharmacists for brand name  
            biologics.  Biologic medicines are currently prescribed to  
            treat blood conditions, cancers, immune disorders such as  
            Rheumatoid Arthritis, Psoriasis and Crohn's Disease and  
            neurological disorders like Multiple Sclerosis and are almost  
            exclusively administered in physician's offices, oncology  
            clinics, specialty pharmacies, hospitals or dialysis centers.   
             Biologics (syringe injectables) are large, complex, protein  
            molecules that consist of one or more chains of amino acids  
            with a complex multi-dimensional structure which makes them  
            difficult to map.  In contrast, pills are traditional chemical  
            medicines with simple molecular structures that are produced  
            by a mechanical and/or chemical process that provide  
            predictable and uniform results. Unlike generic pills, a  
            biosimilar is a "similar" version of the biologic.  It is not  
            generic, the same or identical.  Because of the significant  
            scientific differences between pills and biologics, Congress  
            created a unique and separate legal pathway and regulatory  
            process for the approval of biosimilars. Consequently, the  
            regulatory agencies around the world have deemed that  
            biologics cannot scientifically have "generic or identical  
            versions" and instead can only have "similar" versions, thus  
            the term "biosimilar."  As part of federal health care reform,  
            the Biologics Price Competition and Innovation Act was enacted  
            to allow biosimilars to be approved by the FDA for use in the  
            United States.  In order to reflect the emerging technology of  
            biosimilars and allow for them to be substituted for a  
            biologic, California must update its Pharmacy Practice Act.   
            The Business and Professions Code does not define biosimilars  
            and existing generic pill definitions do not apply.   SB 598  
            allows a pharmacist to substitute a biosimilar medication for  
            a brand biologic when the biosimilar is deemed interchangeable  
            by the FDA.  SB 598 mirrors California's patient protections  
            for generic pill substitution and adds a provision that  
            requires a pharmacist to enter information about the  
            substitution into the patient record system OR notify the  




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            physician within five days after a substitution is made.    
            Notification to the prescribing physician AFTER dispensing  
            does not alter the policy goal of offering alternative, lower  
            cost options for patients.  The purpose of a prescriber  
            notification provision is to provide a record of the  
            substitution, in the event of an adverse reaction, or other  
            clinical responses to the biologic. With biologic medicines,  
            adverse reactions, which occur when a patient's body  
            recognizes a biologic medicine as a foreign matter, may not  
            manifest until 9-12 months after the administration of the  
            drug.  In order to ensure consumer safety, health records  
            should be updated in the event of any contraindications in  
            patients receiving substituted biosimilars. In California,  
            biologics represent .13% of prescriptions dispensed at the  
            retail level.  According to MarketScan, retail pharmacies in  
            California dispense an average of 1.7 biologic prescriptions  
            per week per location.  When compared to the fact that  
            Walgreens pharmacies in California currently perform over four  
            million physician notifications per month for traditional  
            prescriptions, this hardly appears to burden pharmacy staff,  
            especially when weighed against patient safety.

          2.Generics. The FDA defines a generic drug as the same as a  
            brand name drug in dosage, safety, strength, how it is taken,  
            quality, performance, and intended use.  Before approving a  
            generic drug product, FDA requires many rigorous tests and  
            procedures to assure that the generic drug can be substituted  
            for the brand name drug.  According to the FDA, it bases  
            evaluations of substitutability, or "therapeutic equivalence,"  
            of generic drugs on scientific evaluations.  Generic drug  
            products must contain the identical amounts of the same active  
            ingredient(s) as the brand name product.  A drug that is  
            determined to be "therapeutically equivalent" can be expected  
            to have equal effect and no difference when substituted for  
            the brand name product.
            
          3.Biologics.  According to the FDA, biologics are regulated  
            under the federal PHSA while drugs, including insulin and  
            other hormone therapies, are regulated under the FDCA. Both  
            the FDA's Center for Drug Evaluation and Research and Center  
            for Biologics Evaluation and Research have regulatory  
            responsibility for therapeutic biological products, including  
            premarket review and oversight.  Following initial laboratory  
            and animal testing that show the use of a particular  
            biological product in humans is reasonably safe, biological  




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            products (like other drugs), can be studied in clinical trials  
            in humans under an investigational new drug application.  If  
            trials and studies demonstrate that a product is safe and  
            effective for its intended use, the FDA may then approve the  
            market of a biologic by granting a biologics license.

          4.Biosimilars.  According to background information provided by  
            the author and stakeholders, both in opposition to and support  
            of this bill, biologics are large, complex protein molecules  
            used in the treatment, diagnosis or prevention of disease.   
            These are different from small molecule drugs, pills, which  
            are not as structurally complex and are instead relatively  
            simple, organic substances produced by chemical methods.   
            Biologic medicines, on the other hand, are made in living  
            organisms to produce proteins by genetically modifying cell  
            constructs or cell lines.  

            Biosimilars are similar but not identical versions of the  
            original biologic.  The active ingredient of a biosimilar is  
            expected to closely resemble that of the original biologic and  
            unlike generic pills which require the active ingredient to be  
            identical, the exact manufacturing process of an original  
            biologic cannot be exactly duplicated.  Biosimilars are not  
            clinically identical to their reference products.  Biosimilars  
            have been defined by the World Health Organization as "a  
            biotherapeutic product which is similar in terms of quality,  
            safety and efficacy to an already licensed biotherapeutic  
            product," by the European Medicines Agency as a "copy version  
            of an already authorized biological medicine product with  
            demonstrated similarity in physiochemical characteristics,  
            efficacy and safety, based on a comprehensive comparability  
            exercise," and by the FDA as a biological product which is  
            "highly similar to the reference product notwithstanding minor  
            differences in clinically inactive components and for which  
            there are no clinically meaningful differences between the  
            biological product and the reference product in terms of  
            safety, purity and potency of the product".    

            In response to increases in an aging population and larger  
            numbers of patients suffering from chronic disease, there has  
            been a rise in use of biologics, and accordingly a rise in the  
            production efforts of biosimilars.  Biosimilars go through an  
            extensive review process and manufacturers are required to  
            submit immense studies and data demonstrating a products'  
            efficacy and ensuring it is safe for use by consumers.   
            Manufacturers also have to establish ongoing monitoring  




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            programs to ensure the safety of biosimilars.  While  
            biosimilars are currently available in the EU, and other  
            nations are in the process of adopting guidelines and  
            regulatory processes, biosimilars are still a relatively new  
            option in the larger health care delivery and treatment  
            conversation.  

            A pathway for biosimilar regulation in the U.S. was  
            established as a provision of the ACA and in 2012 the FDA  
            issued draft guidelines for biosimilars.  The guidance  
            included which types of studies manufacturers should undertake  
            in order to ensure product safety, potency and purity.   
            However, there is no definitive timeline or date by which  
            biosimilars will be available on the market in the U.S.. 

          5.Related legislation.  AB 1139 (Lowenthal) permits a pharmacist  
            to substitute a biosimilar for a biological product if the  
            product is deemed by the FDA to be interchangeable with the  
            biological product.  The bill is scheduled to be heard in the  
            Assembly Committee on Business, Professions and Consumer  
            Protection on April 30, 2013.   

          6.Double referral. This bill was heard in the Senate Business,  
            Professions, and Economic Development Committee on April 8,  
            2013, and passed with a 10-0 vote.
            
          7.Support.  Supporters of this bill include biologic and  
            biosimilar manufacturers, representatives of chronically ill  
            patients, alliances of physician and research groups, as well  
            as organizations for California's life sciences community who  
            believe that it is a common sense measure which will ensure  
            patient safety without delaying the introduction of  
            biosimilars to the California market.  Supporters highlight  
            the differences between biosimilars and other generic drugs,  
            resulting in a need for prescriber notification to ensure  
            accurate patient records are maintained.  Supporters believe  
            that substitution of biosimilars for biological products will  
            improve patient access to these often life-saving medicines,  
            but note that there need to be certain accountability measures  
            taken, given the unique and very sensitive nature of these  
            drugs.  Supporters agree that the prescriber notification  
            guarantees that physicians maintain knowledge about what  
            medication their patients receive.  BayBio and Biocom write in  
            support, noting that physicians are individuals with the  
            closest relationship to patients and the most knowledge about  




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            a patient's medical condition and treatment regimen, thus  
            should know about a substitution of a prescribed biological  
            product.  BayBio and Biocom believe that biosimilars will  
            provide patients and prescribers with cost savings options and  
            that the provisions in this bill will guarantee patient safety  
            and promote transparency.  Labor groups like the International  
            Union of Operating Engineers and State Building and  
            Construction Trades believe that biologics have improved the  
            quality of life for many members and that their good health  
            will be further promoted with the protections set forth in  
            this bill.  The Pharmaceutical Research and Manufacturers of  
            America believes this bill contains important safeguards that  
            will protect patients and properly inform physicians in the  
            event of an adverse reaction or change in a patient's chronic  
            condition.   

          8.Oppose.  Opponents to this measure, including manufacturers of  
            generic drugs, health plans and retailers, argue that this  
            bill creates barriers to biosimilars entering the California  
            market, will restrict insurers' ability to provide affordable  
            options to patients and that California is unnecessarily  
            making changes before the FDA has weighed in on the issue of  
            substituting biosimilars.  Hospira, Teva Pharmaceuticals,  
            Inc., Boehringer Ingelheim and the Generic Pharmaceutical  
            Association believe that SB 598 is premature and is intended  
            to create doubt about the safety and effectiveness of  
            affordable biosimilar drugs and will prevent patients from  
            accessing more cost-effective, lifesaving medications.  Kaiser  
            Permanente notes that the organization would be able to comply  
            with the provisions of this bill but that it does not support  
            public policy which provides artificial and unnecessary  
            barriers to safe and low cost alternatives for patients.   
            Health Access California writes that the use of generics has  
            helped to control health costs even as prescription drugs have  
            become an even bigger share of health care costs and that  
            there is no reason to create additional barriers to the  
            prescribing of biosimilar drugs beyond those in place for  
            generic drugs. The California Retailers Association and CVS  
            Caremark are concerned that there is not a clear public policy  
            rationale for pharmacies being required to keep records of  
            biosimilars dispensed and that physician notification  
            increases pharmacist workload.  Blue Shield states that this  
            bill contains a provision that only allows for substitution if  
            the biosimilar product costs the patient less, which wile  
            seemingly pro-consumer, would be a de facto ban on biosimilar  
            substitution because there are not separate cost sharing rules  




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            in the standardized benefit designs established by the  
            California Health Benefit Exchange.  

           SUPPORT AND OPPOSITION  :
          Support:  AIM Melanoma
                    Alliance for Patient Access
                    Alliance for Safe Biologic Medicines
                    Alliance of Specialty Medicine
                    American Academy of Dermatology
                    American Academy of Facial Plastic & Reconstructive  
               Surgery
                    American Association of Neurological Surgeons
                    American Association of People with Disabilities
                    American Autoimmune Related Diseases Association
                    American College of Mohs Surgery
                    American Council on Science and Health
                    American Gastroenterological Association
                    American Society of Cataract and Refractive Surgery
                    American Society of Echocardiography
                    American Society of Plastic Surgeons
                    American Urological Association
                    Amgen
                    Association of Black Cardiologists
                    Association of Clinical Research Organizations
                    Association of Gastrointestinal Motility Disorders,  
               Inc.
                    BayBio
                    BIOCOM
                    Biotechnology Industry Organization
                    Blue Ribbon Advocacy Alliance
                    California Healthcare Institute
                    California State Association of Electrical Workers
                    California State Pipe Trades Council, 
                    Coalition of State Rheumatology Organizations
                    Colon Cancer Alliance
                    Colorectal Cancer Coalition
                    Congress of Neurological Surgeons
                    CONNECT
                    Genentech
                    Global Healthy Living Foundation
                    HealthHIV
                    Interamerican College of Physicians and Surgeons
                    International Cancer Advocacy Network
                    International Myeloma Foundation
                    International Union of Operating Engineers




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                    Kidney Cancer Association
                    MANA
                    Merck & Co., Inc.
                    National Alliance on Mental Illness
                    National Physicians Biologics Working Group
                    North American Spine Society
                    Pharmaceutical Research and Manufacturers of America
                    RetireSafe
                    Society for Cardiovascular Angiography and  
               Interventions
                    Society for Excellence in Eyecare
                    State Building and Construction Trades Council
                                                                    TechNet
                    UCB, Inc.
                    Western States Council of Sheet Metal Workers

          Oppose:   Anthem Blue Cross
                    Boehringer Ingelheim
                    California Association of Health Plans
                    CA Conference Board of the Amalgamated Transit Union
                    CA Conference of Machinists
                    California Retailers Association
                    California Teamsters Public Affairs Council
                    CVS Caremark
                    Engineers & Scientists of CA, IFPTE Local 20
                    Express Scripts
                    Generic Pharmaceutical Association
                    International Longshore & Warehouse Union
                    Kaiser Permanente
                    Mylan Labs
                    National Association of Chain Drug Stores
                    Novartis Pharmaceuticals
                    Professional and Technical Engineers, IFPTE Local 21
                    Teva Pharmaceutical Industries, Ltd.
                    UNITE-HERE, AFL-CIO
                    United Food and Commercial Workers Western States  
               Council
                    Utility Workers Union of America, Local 132
                    Walgreens

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